Adrenomyeloneuropathy - 33 Studies Found
Recruiting |
: A Phase 2/3 Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy (CALD) : Cerebral Adrenoleukodystrophy (CALD) : 2013-03-22 : Genetic: Lenti-D Drug Product Lenti-D Drug Product (autologous CD34+ cell-enriched population that conta |
Recruiting |
: A Pilot Study of Vitamin D in Boys With X-linked Adrenoleukodystrophy : X-linked Adrenoleukodystrophy : 2015-10-29 : Dietary Supplement: vitamin D3 Daily oral supplement provided by study investigators |
Completed |
: Exercise Study of Function and Pathology for Women With X-linked Adrenoleukodystrophy : X-linked Adrenoleukodystrophy : 2012-05-07 : Behavioral: exercise training The exercise program uses a local Curves® gym to provide an individua |
Enrolling by invitation |
: Long-term Follow-up of Subjects With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product :
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Recruiting |
: Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD) :
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Recruiting |
: Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy :
: 2015-08-12 : Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f |
Not yet recruiting |
: Early Diagnosis Of Childhood Cerebral ALD : Adrenoleukodystrophy : 2016-10-25 |
Terminated |
: Study of Bile Acids in Patients With Peroxisomal Disorders :
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Completed |
: Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid :
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