Search for Clinical Trial Results

Anemia, Hypoplastic, Congenital - 83 Studies Found
Status | Study |
Active, not recruiting |
Study Name: Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia Condition:
Date: 2011-05-20 Interventions: Drug: leucine Dosage of leucine will be dependent on body |
Completed |
Study Name: Rituximab to Treat Moderate Aplastic Anemia, Pure Red Cell Aplasia, or Diamond Blackfan Anemia Condition:
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Terminated |
Study Name: A Study to Determine Whether Therapy With Daclizumab Will Benefit Patients With Bone Marrow Failure Condition:
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Recruiting |
Study Name: Safety and Efficacy Study of Sotatercept in Adults With Transfusion Dependent Diamond Blackfan Anemia Condition: Diamond Blackfan Anemia Date: 2011-10-31 Interventions:
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Completed |
Study Name: Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia Condition: Fanconi Anemia Date: 2009-08-24 Interventions: Drug: Etanercept All qualified subjects receive 24 weekly subcutaneous injections of Etanercept. |
Recruiting |
Study Name: Diamond Blackfan Anemia Registry (DBAR) Condition:
Date: 2005-03-18 |
Recruiting |
Study Name: L-leucine in Diamond Blackfan Anemia Patients Condition: Diamond Blackfan Anemia Date: 2015-02-18 Interventions: Drug: L-leucine L-leucine pills per os for 6 months |
Recruiting |
Study Name: Improving the Results of Bone Marrow Transplantation for Patients With Severe Congenital Anemias Condition:
Date: 2003-05-29 Interventions:
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Completed |
Study Name: Mobilization of Stem Cells With G-CSF for Collection From Patients With Diamond-Blackfan Anemia Condition: Diamond Blackfan Anemia Date: 2001-02-22 Interventions:
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Completed |
Study Name: Partially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory Cytopenias Condition:
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